I do not have this disease, but I am happy to hear of the trial ... most have emphysema or something similar. The alpha-1 antitrypsin protein is there to reduce inflammation and keep the immune system ...
Beam Therapeutics Reports Third Quarter 2024 Financial Results and Progress Across Priority Programs
In our in vivo portfolio, the BEAM-302 clinical program in alpha-1 antitrypsin deficiency is ... trial for BEAM-301 in glycogen storage disease type 1a (GSDIa), with patient dosing expected ...
Rarely, the skin may be affected as well. When this condition affects the lungs, it causes emphysema, a form of chronic obstructive pulmonary disease. Alpha-1-antitrypsin (AAT) is a protein produced ...
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