Design Therapeutics' GeneTAC platform is revolutionizing genetic disease treatment with small molecules and promising results ...

Initiation of Phase 1b study using SGT-212 for the treatment of patients with Friedreich's Ataxia expected in 2H25. Click ...

A Livingston man will be taking on the Edinburgh half-marathon to raise money for a Craigshill girl who’s been dignosed with ...

Eight-year-old Ella-Rose Kennedy has Friedreich ataxia – a consider which causes damage to the nervous system and cerebellum, ...

Turkish and European researchers will collaborate on the treatment of brain diseases and patient care through new projects ...

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The study, called TRACK-FA, “is a natural history study that investigates brain and spinal cord changes in individuals with Friedreich ataxia,” a rare genetic disease that causes progressive nervous ...

Learn more about whether Ionis Pharmaceuticals, Inc. or PTC Therapeutics, Inc. is a better investment based on AAII's A+ Investor grades, which compare both companies' key financial metrics.

The Maharashtra government noted that high number of cases in certain areas appears to be linked to suspected water ...

Peripheral Nervous System (PNS): The part of the nervous system that lies outside the brain and spinal cord, including nerves and ganglia. Ataxia: A neurological sign characterized by a lack of ...

Sep. 5, 2024 — A study investigated the origin of ataxia in the brain of patients ... Novel Immunotherapy Improves Recovery from Spinal Cord Injury Sep. 4, 2024 — Researchers have designed ...