At 9 months of age he appeared pale. Anemia was found, and electrophoresis established the diagnosis of sickle-cell disease. Both parents had hemoglobin-AS pattern on electrophoresis but were ...
Only a few patients have undergone an intensive gene therapy cure for sickle cell disease since it was approved by the FDA due to it's high cost and limited access. NBC News' Yamiche Alcindor spoke ...
The Congressional Budget Office said policies to increase treatment uptake could affect Medicaid, Social Security, and other government programs.