New discoveries about the severe developmental disorder known as Rett syndrome could open the door to better treatments for the devastating, life-shortening condition.

Cannabidiol is under clinical development by Jazz Pharmaceuticals and currently in Phase II for Rett Syndrome.

Eva Rizzo is able to gain a sense of independence when she partners with her horse at Sebastian Riding Associates in Collegeville.

Scientists investigating the severe developmental disorder known as Rett syndrome have discovered a series of crucial molecular changes that occur long before symptoms appear. The findings could ...

Kemry Smith, a Utah girl, passed away from Rett syndrome, a rare disorder. Her mother, Natalie Smith, described Kemry as kind, caring and emotionally intuitive. Family, friends, and strangers ...

Long-term clinical profiles of female patients with classic Rett syndrome are presented and exemplified by three cases, as experienced over four decades. Emphasized is the frequently surprisingly ...

Fintel reports that on January 3, 2025, Guggenheim downgraded their outlook for ACADIA Pharmaceuticals (NasdaqGS:ACAD) from ...

Taysha Gene Therapies, Inc. (Nasdaq: TSHA) (Taysha or the Company), a clinical-stage biotechnology company focused on ...

Neurogene has halted patient enrolment in the high-dose arm of its trial of Rett syndrome gene therapy, sparking another run on its shares. Last week, the company reported that NGN-401 had shown ...