Major positive events in 2024 include India’s first solar-powered remote village, the discovery of plastic-decomposing worms, ...

4D-310 is under development for the treatment of Fabry disease. The drug candidate is administered through intravenous route. The drug candidate is based on vector evolution platform technology that ...

Sangamo (SGMO) stock faces challenges as Pfizer terminates partnership for hemophilia A gene therapy, impacting share price ...

Amicus Therapeutics' shares are down 15% recently despite a profitable Q3 2024 and raised FY2024 outlook. Click here to find ...

An update from JCR Pharmaceuticals Co., Ltd. ( (JP:4552) ) is now available.

JCR Pharmaceuticals Co., Ltd. ( (JP:4552) ) has issued an update.

Brian has Fabry disease, a lysosomal storage disorder that can cause a variety of symptoms. “It's a condition where your cells are not able to break down a certain substance, and that ...

Jennifer Wound of Genzyme illustrates the power of using film in rare disease awareness campaigns by discussing Genzyme's 'Facing Fabry Together' patient video. Disease awareness campaigns ...

"We are committed to delivering innovative therapies and solutions for people living with Fabry disease, their families and caregivers." A biopharmaceutical company, Protalix leverages its plant ...

Additionally, full data for the treatment of Fabry disease is expected in the first half of 2025, with a potential BLA filing in the second half of the year. This progress may make Sangamo an ...

INR:8147. monsters meaning A new drug for rare diseases urgently needed in clinical practice, "Agalsidase α", has been approved in China to treat Fabry disease ...

INR:4654. faridabad weekly chart 2023 FDA granted priority review for innovative treatment of Fabry disease, expected to be approved early next year H ...