Onlymyhealth6d
What Is Sanfilippo Syndrome: Symptoms, Treatment, and the Impact on Children’s Lives
Discover Sanfilippo Syndrome a rare genetic disorder affecting childrens development Learn about its symptoms treatment ...
Fox Carolina28d
Clemson researchers conducting breakthrough research on childhood Alzheimer’s
Researchers have identified four drugs already on the market and are testing them to see if they work against Sanfilippo syndrome. “They are approved for something else currently, but they are ...
Nasdaq1mon
Ultragenyx Submits BLA To FDA For UX111 Gene Therapy For Sanfilippo Syndrome Type A
If approved, UX111 would be the first approved therapy in the U.S. for Sanfilippo Syndrome Type A. RARE closed Wednesday's (Dec.18.2024) trading at $42.94, down 4.47%. In premarket trading ...