Some types of muscular dystrophy typically ... Duchenne muscular dystrophy occurs when that gene fails to make dystrophin. Becker muscular dystrophy occurs when a different mutation in the same ...
There are several types of muscular dystrophy ... which can be life-threatening. The symptoms of Becker muscular dystrophy are similar to those of Duchenne muscular dystrophy.
On the basis of these findings and clinical experience, individuals with Becker muscular dystrophy (BMD) are advised to avoid excess physical exertion. Sveen et al. have performed the first study ...
While the last decade has brought considerable progress for patients with DMD, substantial unmet need remains. Several ...
A pilot study in 19 LGMD patients and one with Becker MD found low-dose prednisone helped lower markers of muscle damage and ...
Muscular Dystrophy (MD) is a genetic condition causing progressive muscle weakness and complications in vital organs. Early ...
In recent years, a growing understanding of myotonic dystrophy type 1 (DM1)—an often fatal ... Like many other muscular dystrophies, the cause of DM1 is genetic. An alteration in the causative ...
Ips Heart Inc. has been awarded orphan drug designation by the FDA for its GIVI-MPC stem cell therapy for Becker muscular dystrophy. GIVI-MPC has the unique ability to create new muscle with full ...
We identified one particular microRNA, miR-486, as a muscle-enriched miRNA that is strongly reduced in expression levels in Duchenne muscular dystrophy (DMD), but not the milder Becker muscular ...
Pfizer is “evaluating appropriate next steps” for its Duchenne muscular dystrophy (DMD ... toward advancing therapies for Duchenne and Becker, and we draw strength from the resilience and ...